Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY) announced today that the U.S. Food and Drug Administration (FDA) has accepted the company's supplemental Biologics License ...

PNH can develop at any age ... on RBCs linked to PIGA gene mutation. Additional tests, such as coagulation studies and renal function tests, assess complications, while bone marrow biopsy and ...

Having two copies of the MTHFR gene mutation may raise your risk for certain health conditions, though more research is needed. You may have the mutation and not find out unless you undergo ...

Panelists discuss how they maintain treatment adherence through digital health apps, calendar reminders, and symptom journals while working closely with their care teams to address uncertainties and ...

The lifetime risk of thrombosis in patients with PNH is approximately 50%, and it tends to be found in the abdominal or cerebral veins. Patients who experience thromboses at unusual sites should be ...

Jace, 6, was born with a rare and aggressive eye condition An experimental trial of gene therapy has helped four toddlers - born with one of the most severe forms of childhood blindness - gain ...

Building a gene editor took months. With CRISPR even high-schoolers can get hold of editing systems in the time it takes to order RNA sequences online and have them shipped by FedEx. In a short ...

Pfizer’s decision to halt further marketing of Beqvez is further sign of the sparse patient interest in gene therapies for the bleeding condition. Rapid scientific advances have put the gene therapy ...

Benign paroxysmal positional vertigo (BPPV) is a type of vertigo caused by calcium crystals in the inner ear. These crystals are usually located in two parts of the ear called the utricle and saccule.

the Deputy Spokesperson of the National Police of Haiti (PNH), gave an update on the operations carried out against armed gangs in the West department, particularly in the communes of Kenscoff and ...