Is your urine color hiding a dangerous disease? Uncovering PNH
Paroxysmal nocturnal hemoglobinuria (PNH) is a rare disease that affects red blood cells, causing symptoms like dark urine, ...
pharmaphorum3d
Roche gets first world okay for PNH drug crovalimab
China has become the first country in the world to approve Roche’s anti-complement C5 antibody crovalimab, the only treatment for the rare disorder paroxysmal nocturnal haemoglobinuria (PNH ...
pharmaphorum7d
Novartis' oral drug iptacopan tops injectables in head-to-head PNH trial
The latest positive readout comes from the APPLY-PNH study, which pitted iptacopan against AstraZeneca/Alexion's anti-C5 antibodies Soliris (eculizumab) and Ultomiris (ravulizumab) in adults with ...
Yahoo Finance28d
Novartis receives Health Canada approval for Fabhalta® oral treatment for adult patients with PNH
Significant unmet need remains in PNH, a chronic, rare and potentially life-threatening blood disorder; a large proportion of patients can remain anemic and dependent on blood transfusions 3,4 ...
Newswire28d
Novartis receives Health Canada approval for Fabhalta® oral treatment for adult patients with PNH
Gene ID: 727. National Library of Medicine ... Twice Daily LNP023 in Adult Patients With PNH and Residual Anemia, Despite Treatment With an Intravenous Anti-C5 Antibody. clinicaltrials.gov ...
Indiatimes14d
Is your urine color hiding a dangerous disease? Uncovering PNH
PNH can develop at any age ... on RBCs linked to PIGA gene mutation. Additional tests, such as coagulation studies and renal function tests, assess complications, while bone marrow biopsy and ...