For example, if a child has coarse facial features and developmental delays, a pediatrician may have reason to believe that the child has a form of mucopolysaccharidosis. Mucopolysaccharidosis is ...
Under the terms of the agreement, Regenxbio and Nippon Shinyaku will develop and commercialize RGX-121 for Mucopolysaccharidosis II, also known as Hunter syndrome and RGX-111 for ...