News Medical on MSN1d
Pioneering the world’s first CRISPR medicine for sickle cell disease
When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters ...
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UK first to approve Vertex, CRISPR drug for blood disorders
cleared Vertex Pharma and CRISPR Therapeutics' Casgevy (exagamglogene autotemcel or exa-cel) in Great Britain as a one-shot therapy that involves harvesting bone marrow stem cells from patients ...
Bahrain Makes History with First Successful CRISPR-Based Sickle Cell Treatment Outside the US
This achievement follows Bahrain’s landmark decision on 2 December 2023 to become the second country globally and the first in the Middle East to approve Casgevy for the treatment of SCD and TDT. The ...