This new tool, known as minimal, versatile genetic perturbation technology (mvGPT), combines the powers of gene editing, ...

A £1.65 million treatment has been approved for use for some NHS patients, offering some with an inherited blood disorder ...

Base editing utilizes enzymes to modify single amino acids at the most foundational unit of DNA, called a base.

Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...

A gene-edited mouse with two male parents has survived to adulthood, pushing new progress on stem cell research.

The National Institute for Health and Care Excellence (NICE) has approved a one-off gene editing therapy to treat severe sickle cell disease (SCD) in people 12 years and over. In final draft guidance1 ...

NHS patients with sickle cell disease will be able to benefit from a groundbreaking gene-editing treatment that offers the prospect of a cure for the condition. The one-off gene therapy, known as ...

People in England to benefit from groundbreaking one-off gene therapy for severe sickle cell disease approved by NICE ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and ...

The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...

Every time a shuttle docks with the International Space Station (ISS), a delicate dance unfolds between the shuttle's docking ...

Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...