RIKEN researchers have discovered how a single mutation in one gene can simultaneously result in two symptoms—a severely ...

Proteins are the building blocks of life. They consist of folded peptide chains, which in turn are made up of a series of ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...

Converging computational and laboratory technologies are helping anti-cancer immune responses hit their target more effectively.

Mitochondrial diseases, arising from mutations in mitochondrial DNA (mtDNA), are a diverse group of disorders that lead to ...

Gene therapy for cystic fibrosis is advancing fast. Explore key biotech players, clinical progress, and its potential to ...

Organoids are made to model human organs and are promising for research and therapy, but there are limitations to their ...

Fibrobiologics' cell therapy CYMS101 significantly increased myelin production and promoted myelin repair in a mouse model of ...

Collaborative research defines a novel approach to understanding how certain proteins called transcription factors determine which genetic programs will drive cell growth and maturation. The method, ...

Find out what happens to heart cells in space and how their adaptation could revolutionize heart disease treatment.

Summary: Collaborative research led by investigators at Dana-Farber/Boston Children's Cancer and Blood Disorders Center defines a novel approach to understanding how certain proteins ... blood cells ...