Ultomiris is already approved for PNH and aHUS and in late-stage development ... Wilson Therapeutics and Portola and forging an alliance with gene-silencing specialist Dicerna focusing on ...

Gene was suffering from severe heart disease and advanced Alzheimer's disease, while Betsy suffered from hantavirus, which is spread through rodent droppings Gene Hackman's wife Betsy Arakawa ...

The mystery surrounding Oscar-winning actor Gene Hackman's death has been solved. The 94-year-old died of heart disease and complications caused by Alzheimer’s disease, according to the New ...

China has become the first country in the world to approve Roche’s anti-complement C5 antibody crovalimab, the only treatment for the rare disorder paroxysmal nocturnal haemoglobinuria (PNH ...

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

One of the most highly anticipated FDA decisions this month is for Alnylam Pharmaceuticals, which is seeking to expand the ...

Gene expression is the generation of a functional gene product from the information encoded by a gene, through the processes of transcription and translation. Gene products are often proteins ...

It seeks to understand the process of trait inheritance from parents to offspring, including the molecular structure and function of genes, gene behaviour in the context of a cell or organism (e.g ...

SANTA FE, N.M. — Forensic experts came to a heartrending conclusion Friday about the manner of death for actor Gene Hackman: he died of heart disease with complications from Alzheimer's disease ...

After that, the next step in CRISPR gene editing is usually to alter that piece of DNA. However, CRISPR has also been adapted to do other things too, such as turning genes on or off without ...

Learn the lifestyle tips you can follow to care for your physical and mental health when you have paroxysmal nocturnal hemoglobinuria (PNH).

Jay T. Rubinstein, MD, PhD, highlighted promising CHORD trial data showing that DB-OTO gene therapy has led to hearing improvements in treated participants. New data from the CHORD trial (NCT05788536) ...