Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...

Just a few weeks France's Sanofi made a $40 million investment in Gyroscope for first refusal rights on the gene therapy – called GT005 – but it is Novartis that has swooped on the company and ...

The Medical University of South Carolina Health has established the Rena N. Grant Sickle Cell Center to help treat those ...

Cell and gene therapy is the hottest area in biotech at the moment, and Gilead’s $11.9bn acquisition of Kite Pharma in October has been followed by Celgene’s $9bn buyout of Juno Therapeutics.

The Bermuda National Trust [BNT] held its Plant & Bake Sale this weekend, offering a diverse selection of plants, baked goods, and local produce at Waterville on Pomander Road in Paget.

The high-dose Spinraza is Biogen's answer to competitors such as Novartis' gene therapy Zolgensma. Specifically, the combo is approved in Europe for patients with epidermal growth factor receptor ...

It is hoped that larger trials and new research approaches considering OCD heterogeneity, gene function and gene–environment interaction may help to develop a more individualized treatment plan ...

The companies will work together by using the codon-optimized BBS1 AAV9 vector to minimize the vision loss caused by the genetic defects in the BBS1 gene.

Bipolar II Hypomania (4 days) One or more episodes required (2 weeks) Completed suicide in 10% to 15%, school/occupational failure, divorce Substance abuse or dependence, anorexia nervosa, bulimia ...

👉 Novartis' neuroscience research lead, Robert Baloh, highlighted the alignment with the company's goals to tackle inherited neuromuscular conditions and improve existing gene therapy solutions.

Regeneron Pharmaceuticals beat fourth-quarter sales and profit estimates on Tuesday, on continuing demand for its eczema treatment, Dupixent, and announced a dividend and stock buyback program ...