UK health system to offer cutting-edge gene therapy for sickle cell disease
Britain's National Health Service (NHS) will provide a cutting-edge gene therapy that aims to cure sickle cell disease, the ...
Sickle cell disease is a genetic disorder that causes lifelong suffering – here’s what you need to know
Accumulation of clots causes some of the most severe symptoms of sickle cell disease, including strokes, kidney failure, ...
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Sickle cell patients share delight over approval of new treatment
A cutting-edge gene therapy has been approved ... with severe sickle cell disease. Casgevy, also known as exa-cel, was the first treatment to be licensed using gene-editing tool Crispr, which ...
Yahoo News UK12d
Sickle cell patients share delight over approval of new treatment
A cutting-edge gene therapy has been approved for NHS use for some patients with severe sickle cell disease. Casgevy, also known as exa-cel, was the first treatment to be licensed using gene-editing ...
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FDA gives go-ahead for CRISPR-based sickle cell disease trial
Development of a stem cell therapy for sickle cell disease from Vertex and development partner CRISPR therapeutics can go ahead, after the FDA lifted ... have obtained approval for clinical ...
Euronews12d
‘Much-needed hope’ as CRISPR gene editing therapy recommended for sickle cell disease
not only because this marks the first approval of a CRISPR-based gene therapy for SCD [sickle cell disease] in the NHS, but also because it offers a potentially curative treatment for eligible ...