Potent in vivo gene editing in skeletal muscle of non-human primates by a novel, ultracompact CRISPR system delivered via a single AAV vector.

Akribion Therapeutics emerges from stealth with €8 million in seed funding to develop a novel cancer RNA-guided approach ...

Advances in CRISPR technologies promise to accelerate the burgeoning pipeline of gene-editing therapies and broaden access to these disease-altering therapies.

The core components of CRISPR-based genome-editing ... In the future, they hope their methods may also help scientists design delivery vehicles to evade the immune system. More information ...

Every time a shuttle docks with the International Space Station (ISS), a delicate dance unfolds between the shuttle's docking ...

Cell culture is a key technique in scientific research It lets scientists grow and study cells outside their natural environment Knowing how to improve cell viability and growth is important for succe ...

In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches -- gene therapy ...

CRISPR-Cas9 is one of the biggest discoveries of the 21st century ... potentially enhancing safety profiles compared to traditional CRISPR methods. Other CRISPR-based therapies are progressing through ...

Local production decreases transportation and logistics expenses and shortens the time to treatment delivery. The Canadian-Led Immunotherapies ... from gene-editing technologies such as TALEN and ...