When Vijay Sankaran was an MD-PhD student at Harvard Medical School in the mid-2000s, one of his first clinical encounters ...

The company submission assumes that red blood cell transfusions are typically given every 6 weeks ... Then, the CRISPR associated protein 9 is used to edit the BCL11A gene before the cells are frozen.

A new review in Engineering reveals that CRISPR technologies are revolutionizing regenerative medicine. Scientists from ...

A recent review published in the journal Engineering delves into the significant advancements and potential of CRISPR technologies in the field of ...

A gene-editing drug developed by CRISPR Therapeutics and Vertex Pharma has achieved “remarkable” improvements in patients with beta thalassaemia and sickle cell disease in an early-stage trial ...

“We are entering 2025 with strong momentum behind our lead program, pociredir, for the treatment of sickle cell disease,” said Alex C ... of key fetal globin repressors, including BCL11A, thereby ...

Bone marrow transplantation (BMT) can potentially cure sickle cell disease, an inherited and painful blood disorder, but ...

Esther Nkemakolam runs her fingers through kinetic sand and sings a “Moana” song as UPMC Children’s Hospital nurse Taylor ...