Kellogg School of Management13y
A Family Fight Against ALS
The cell can’t repair or maintain itself and becomes severely damaged. “This discovery opens up a whole new field for finding an effective treatment ... and ALS that targets the brain, ALS/dementia.
Nature4y
First licensed stem cell therapy for ALS
Its lead product is NeuroNata-R (lenzumestrocel), the world’s first stem cell-based therapy for amyotrophic lateral sclerosis (ALS). NeuroNata-R was approved as an orphan drug for the treatment ...
pharmaphorum10y
Stem cell therapy for ALS fast-tracked by FDA
A stem cell therapy for amyotophic lateral sclerosis (ALS) could have a shorter route to market after being fast-tracked by the FDA. Israeli firm BrainStorm Cell Therapeutics has been granted the ...
pharmaphorum8d
FDA advisors unconvinced by BrainStorm’s ALS cell therapy
An FDA advisory committee has voted by a huge margin that BrainStorm’s stem cell therapy for amyotrophic lateral sclerosis (ALS) – NurOwn – does not have enough data to support its approval.
FierceBiotech29d
Journey of Voyager's ALS gene therapy to clinic hindered by need to find alternative payload
Voyager Therapeutics no longer expects to sail its amyotrophic lateral sclerosis (ALS) candidate into the clinic in the coming months as the gene therapy company looks to rejig the asset’s payload.
Nature1y
Rapa’s epigenetic reprogramming creates T cell therapies for solid tumors and neurodegeneration
Rapa is developing its RAPA-201 cancer product in parallel to RAPA-501, which is an ALS cell therapy product that has a United States Food and Drug Administration fast track designation.